Emil Kakkis, M.D., Ph.D. - Developing Treatments for Rare Diseases Sanford Burnham Prebys 31:11 13 years ago 322 Скачать Далее
Emil Kakkis, MD, PhD, EveryLife Foundation EveryLife Foundation for Rare Diseases 4:29 11 years ago 105 Скачать Далее
Emil Kakkis, MD, PhD | The Challenges of Managing Heterogeneity in Rare Diseases EveryLife Foundation for Rare Diseases 23:54 5 years ago 410 Скачать Далее
Developing Novel Treatments for Rare Disorders: A Look at MPS I with Dr. Emil Kakkis WCG 19:30 2 months ago No Скачать Далее
Emil Kakkis - keynote lecture: Translating rare disease research into medicine Wellcome Connecting Science Learning and Training 37:08 2 years ago 423 Скачать Далее
Emil Kakkis, MD, PhD - Nov. 13, 2014 RDLA Caucus Briefing EveryLife Foundation for Rare Diseases 6:24 9 years ago 65 Скачать Далее
Emil Kakkis M.D., Ph.D. PKU presentation at Rare Disease Workshop 3 KakkisEveryLife 13:29 12 years ago 123 Скачать Далее
Emil Kakkis, M.D., Ph.D. opening presentation at Rare Disease Workshop 3 KakkisEveryLife 14:24 12 years ago 203 Скачать Далее
Emil Kakkis, M.D., Ph.D. final presentation at Rare Disease Workshop 3 KakkisEveryLife 16:22 12 years ago 64 Скачать Далее
How A Doctor Helped A Young Patient With Fatal Disorder Defy Odds TODAY 5:05 2 years ago 4 691 Скачать Далее
Wait, How Do You Spell That: A Rare Disease Podcast - Dr. Emil Kakkis, Founder of Ultragenyx Patient Worthy 25:13 6 months ago 25 Скачать Далее
Emil Kakkis, M.D., Ph.D. Urinary GAG presentation at Rare Disease Workshop 3 KakkisEveryLife 24:38 12 years ago 109 Скачать Далее
Time for an Ultra-Orphan Drug Act by Dr. Emil Kakkis Cure GM1 Foundation 29:28 11 months ago 200 Скачать Далее
Translational Medicine Symposium 2013: Dr. Emil Kakkis, 3 of 4 Albert Einstein College of Medicine 36:34 10 years ago 709 Скачать Далее
Faster Rare Disease Progress is Within our Reach with Dr. Emil Kakkis and Mary Woolley ResearchAmerica 16:40 2 years ago 203 Скачать Далее
2019 FAST Science Summit on Angelman Syndrome - Keynote, Dr. Emil Kakkis, Ultragenyx Pharmaceutical FAST 51:08 4 years ago 1 153 Скачать Далее
FDA Approval of Crysvita® for X-linked Hypophosphatemia (XLH) HPR 7:05 6 years ago 2 472 Скачать Далее